Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has been challenging. In the latest case, the scientists developed a CRISPR ...
In a groundbreaking development, a baby with a rare metabolic disorder has experienced real-world improvements following a procedure using CRISPR gene-editing technology. This case not only represents ...
(NewsNation) — Doctors used personal gene therapy to treat an infant with a deadly genetic disease in a medical first. KJ Muldoon was born in August of 2024, and DNA sequencing revealed he had ...
He Jiankui, PhD, a Chinese scientist who sparked controversy in 2018 after claiming to have genetically modified two human embryos, is on a new scientific endeavor: trying to develop a therapy for ...
A baby boy with a devastating genetic disease is thriving after becoming the first known person to receive a bespoke, CRISPR therapy-for-one, designed to correct his specific disease-causing mutation ...
Bring up germline editing, and most scientists cringe. The idea behind the notorious CRISPR-baby scandal, editing reproductive cells or embryos tinkers with DNA far beyond just the patient—any changes ...
For most of her life, Victoria Gray, a 37-year-old mother of four from Mississippi, had experienced excruciating bouts of pain. Born with the blood disorder sickle cell disease, lengthy hospital stays ...