Sangamo Therapeutics ran out of cash. Eli Lilly and Astellas want the science it spent decades building.

A gene therapy that instructs cells to produce more of an anti-ageing protein called klotho is about to be offered by a US ...

The FDA will reconsider approving Regenxbio's experimental gene therapy for a deadly and rare childhood brain disorder it ...

From data lakes to streamlined production, Kriya, Opus, and Epicrispr discuss how technology is improving their operations.

With a regulatory route now in place, Regenxbio expects to meet with the FDA again in July, with a BLA resubmission to follow ...

An eight-month-old baby from Israel has become the first human ever to receive an experimental gene therapy designed to replace a missing gene responsible for a devastating neurological disease that ...

Intravenous gene therapy delivering the frataxin gene appears safe and is associated with preliminary signs of reduced heart damage in patients with Friedreich ataxia cardiomyopathy.

Revolutions in gene therapy are rapidly changing the landscape of modern medicine. Revolutions in gene therapy are rapidly changing the landscape of modern medicine, forcing society and science alike ...

Scientists studying aging may be taking an important step toward understanding how to preserve the body's cells as they grow ...

A young man from southeastern Louisiana has become the first in his region to be functionally cured of sickle cell disease, ...

Heart failure has historically been irreversible, but the outcome of a new study suggests that could someday change. At the University of Utah, scientists used a new gene therapy that was shown to ...

A new gene therapy appears to be safe in patients diagnosed with Friedreich ataxia cardiomyopathy, a progressive and fatal ...