Reeves is an associate professor of pediatrics and epidemiology at the University of Michigan and the principal investigator of the Michigan Sickle Cell Data Collection program. In December 2023, a ...
Gene editing has delivered remarkable results against sickle cell disease. Now researchers are working to make these ...
Stable production of anti-sickling adult hemoglobin (HBA T87Q) and elimination or significant reduction of vaso-occlusive events sustained through last follow-up for all evaluable patients (n=38), ...
Motixafortide effectively mobilized sufficient hematopoietic stem cells (HSCs) in patients with sickle cell disease enabling accelerated access to gene therapies 90% (9 of 10) of patients were able to ...
Beam Therapeutics is set to present positive and significant data from the BEACON Phase 1/2 clinical trial of BEAM-101 at a major conference, enhancing visibility and credibility within the scientific ...
On Saturday, Beam Therapeutics Inc. (NASDAQ:BEAM) revealed new safety and efficacy data from its BEACON Phase 1/2 trial of BEAM-101 in patients with sickle cell disease (SCD) with severe ...
A Nashville doctor helped pioneer an FDA approved "state-of-the-art" gene-editing therapy that could be a cure for painful ...
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Agios Pharmaceuticals Shares Rise After FDA Grants Priority Review for Sickle Cell Disease Treatment
Agios Pharmaceuticals shares rose Tuesday after the U.S. Food and Drug Administration granted priority review to the company's supplemental new drug application for mitapivat to treat sickle cell ...
Adam Feuerstein is a senior writer and biotech columnist, reporting on the crossroads of drug development, business, Wall Street, and biotechnology. He is also a co-host of the weekly biotech podcast ...
CAMBRIDGE, Mass., Dec. 02, 2025 (GLOBE NEWSWIRE) -- Fulcrum Therapeutics, Inc.® (Nasdaq: FULC), a clinical-stage biopharmaceutical company focused on developing small molecules to improve the lives of ...
In 2023, 1,430 people with sickle cell disease were hospitalized in Louisiana — 25% were between 20 and 29 years old. Sickle cell disease is a chronic condition that causes intense pain throughout the ...
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