Medical Xpress

What you should know about spinal muscular atrophy

Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...
Healio

Gene therapy improves motor function in spinal muscular atrophy at 52 weeks

We were unable to process your request. Please try again later. If you continue to have this issue please contact [email protected]. Patients treated with onasemnogene abeparvovec recorded ...
Morningstar

FDA Approves New Tablet Form of Evrysdi for Treatment of Spinal Muscular Atrophy

New York, Feb. 12, 2025 (GLOBE NEWSWIRE) -- The Muscular Dystrophy Association (MDA) today celebrates the decision by the US Food and Drug Administration (FDA) to grant approval of a risdiplam ...
Becker's Hospital Review

Patients seeking financial assistance for $750k Biogen drug must sign away PHI

Biogen offers a financial assistance program for its treatment Spinraza but there’s a catch: patients must sign away their protected health information to the company, reports the Waco Tribune-Herald.

Neuromuscular Disease Therapeutics Market to Reach US$ 45.62 Billion by 2033 as Gene Therapies and RNA-based Treatments Redefine Patient Outcomes

The Neuromuscular Disease Therapeutics Market is entering a period of accelerated growth, supported by breakthroughs in gene ...
Local 12 WKRC Cincinnati

5K at Xavier University raise awareness for those living with spinal muscular atrophy

CINCINNATI (WKRC) - The annual "Cure SMA Walk-n-Roll" event kicked off Saturday morning at Xavier University, drawing participants to raise awareness and support for those living with spinal muscular ...