The MDA Engage seminar in Hershey, Pennsylvania, brought together neuromuscular families and specialists for education and ...

Able,” a short film starring my girlfriend, Amanda, and me, was selected for inclusion in AN/OTHER Film Festival in Fremantle ...

The FDA is considering whether to conditionally approve a new treatment for DMD patients with mutations amenable to exon 51 ...

After two difficult years, columnist Betty's Vertin's son Max won't go back to college this fall, a decision that has her breathing easier.

Commendamide, a metabolite produced by beneficial gut bacteria that are depleted in people with DMD, protects muscle cells ...

CureDuchenne has launched a national public service announcement campaign to highlight the urgent need for new treatments for ...

We are pleased to partner with the Muscular Dystrophy Association (MDA) to bring you coverage from the MDA Engage Symposium.

There are 24 hours in a day, so there should be enough time in each one to keep from feeling caregiver burnout, says columnist.

Two major steps are now complete in an early clinical trial testing a one-time epigenetic therapy — a treatment designed to turn on or off a specific gene without changing the underlying DNA — for ...

There’s a certain rhythm to gardening that I’ve always loved. The early mornings, the quiet work of turning soil, the satisfaction of seeing something grow because you cared for it. In my backyard, ...

Last month, the Purple Parade featured my story on its website. Reading my profile prompted me to reflect on why I continue speaking up about living with Duchenne muscular dystrophy (DMD) and what I ...